Cureus | Efficacy and Safety of Luspatercept in the Treatment of β- Thalassemia: A Systematic Review | Article
Frontiers | Genetic and Epigenetic Therapies for β-Thalassaemia by Altering the Expression of α-Globin Gene
JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?
Gene therapies for transfusion dependent β‐thalassemia: Current status and critical criteria for success - Soni - 2020 - American Journal of Hematology - Wiley Online Library
Β-Thalassemias | NEJM
Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis
Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon | Article
Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review
Quality of life in patients with β‐thalassemia: A prospective study of transfusion‐dependent and non‐transfusion‐dependent patients in Greece, Italy, Lebanon, and Thailand - Cappellini - 2019 - American Journal of Hematology - Wiley
Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia: Molecular Therapy
A systematic review of quality of life in sickle cell disease and thalassemia after stem cell transplant or gene therapy - ScienceDirect
Β-Thalassemias | NEJM
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library
Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th Edition - Version 2.0) by Thalassaemia International Federation (TIF) - Issuu
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Cureus | Blood Demand and Challenges for Patients With Beta-Thalassemia Major in Eastern Saudi Arabia | Article
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Survival and complications in patients with haemoglobin E thalassaemia in Sri Lanka: a prospective, longitudinal cohort study - The Lancet Global Health
Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Frontiers | New Insights Into Pathophysiology of β-Thalassemia
Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library
